Frontiers | Recommendations for Infantile-Onset and Late-Onset Pompe Disease: An Iranian Consensus
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine
The impact of antibodies on clinical outcomes in diseases treated with therapeutic protein: Lessons learned from infantile Pompe disease | Genetics in Medicine
Representative Western gel blot showing CRIM negative s | Open-i
Algorithm for the Early Diagnosis and Treatment of Patients with Cross Reactive Immunologic Material- Negative Classic Infantile
Pompe disease treatment: What are the options? | Pompe Disease News
Characterization of immune response in Cross-Reactive Immunological Material (CRIM)-positive infantile Pompe disease patients treated with enzyme replacement therapy - ScienceDirect
Targeted approaches to induce immune tolerance for Pompe disease therapy: Molecular Therapy Methods & Clinical Development
Kaplan-Meier curve for overall survival of CRIM-negative IPD patients... | Download Scientific Diagram
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine
Pompe Disease
CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy | Genetics in Medicine
Enzyme therapy and immune response in relation to CRIM status: the Dutch experience in classic infantile Pompe disease | Journal of Inherited Metabolic Disease
IJNS | Free Full-Text | Newborn Screening for Pompe Disease: Pennsylvania Experience
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction - ScienceDirect
CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy - ScienceDirect
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
Algorithm for the Early Diagnosis and Treatment of Patients with Cross Reactive Immunologic Material-Negative Classic Infantile Pompe Disease: A Step towards Improving the Efficacy of ERT | PLOS ONE
Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
Children | Free Full-Text | The Clinical Management of Pompe Disease: A Pediatric Perspective
Treatment approach for IOPD. CRIM, cross-reactive immunologic... | Download Scientific Diagram
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
Efficacy of ERT+ITI in CRIM-negative IPD patients treated in the... | Download Table
Early ERT Key in Severe Classic Infantile Pompe, Study Finds
